Sesión XII. Dra. María José de Castro.

SIMPOSIO MEDSCAPE/ULTRAGENIX: Clinician and Patient Perspectives in the Management of Long-Chain Fatty Acid Oxidation Disorders. GARROD AWARD LECTURE. SIMPOSIO TRAVERE: Classical Homocystinuria and Development of a New Enzyme Replacement Therapy....

Sesión XI. Dr. Domingo González-Lamuño.

PLENARY SESSION 1: Environment meets Metabolism. Introduction into the session. Genetics and the microbiome. Exercise testing and prescription in metabolic diseases SIMPOSIO TAKEDA: Optimizing early diagnosis in lysosomal storage diseases and...

Sesión X. Dr. Antonio González-Meneses.

SIMPOSIO SANOFI: Olipudase alfa: a new treatment for patients with ASMD. PARALLEL SESSION 2D: Novel Diagnostic Technologies.  SIMPOSIO ASTELLAS: Pompe Disease: A Metabolic Disease Impacting Muscle and Potential Muscle-directed Gene Therapeutic...

Sesión IX. Dr. Isidro Vitoria.

EHOD MEETING. PARALLELL SESSION 1C: Glycosylation and Carbohydrate Disorders. PARALLEL SESSION 4B: Urea cycle disorders.